Firefly Fund is a global leader in providing support, resources, and reassurance to families living with rare neurodegenerative genetic diseases like Niemann-Pick Disease Type C that affect children and currently have no cure. Headquartered in Austin, Texas, Firefly Fund works directly with researchers, physicians, and patients through its three main initiatives: Newborn Screening, Translational Medical Research, and the Patient Access Fund. A rare disease diagnosis is unimaginable, but together we will find a cure.