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Articles from March, 2021

Firefly Chat Episode 7 (Part 2): NPC Moms React to Adrabetadex News

A continuation of Firefly Fund co-founder Pam Andrews’ discussion with NPC moms, highlighting the benefits of Adrabetadex. The moms share their fears about a future without the medication, the popular…Read More

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  • Austin’s IntraBio Gets FDA Approval for Niemann-Pick Type C1 Treatment
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